Janel R. Long-Boyle, PharmD, PhD1; Donald B.
Kohn, MD2; Ami J. Shah, MD3; Sueli
Marques Spencer, PhD4; Julian Sevilla, MD,
PhD5; Claire Booth, MBBS, PhD,
FRCPCH6; José Luis López Lorenzo,
MD7; Eileen Nicoletti, MD4; Arpita
Shah, PharmD4; Meredith Reatz4;
Joana Matos, PhD4; Jonathan D. Schwartz,
MD4
1 University of California, San Francisco, San
Francisco, CA,
2 University of California, Los Angeles, Los Angeles,
CA,
3 Lucile Packard Children’s Hospital, Stanford
University School of Medicine, Stanford, CA, US
4 Rocket Pharmaceuticals, Inc., Cranbury, NJ, US
5 Hematología y Hemoterapia, Fundación para la
investigación Biomédica, Hospital Infantil Universitario Niño Jesús
(HIUNJ), Madrid, Spain
6 University College of London, Great Ormond Street
Hospital, Institute of Child Health, and Great Ormond Street Hospital
NHS Foundation Trust, London, UK
7 Instituto de Investigación Sanitaria Fundación
Jiménez Díaz (IIS-FJD), Hospital Universitario Fundación Jiménez Díaz,
Madrid, Spain
Corresponding author :
Jonathan D. Schwartz, MD
Rocket Pharmaceuticals, Inc.
9 Cedarbrook Drive
Cranbury, NJ 08512
js@rocketpharma.com
646-440-9123