Janel R. Long-Boyle, PharmD, PhD1; Donald B. Kohn, MD2; Ami J. Shah, MD3; Sueli Marques Spencer, PhD4; Julian Sevilla, MD, PhD5; Claire Booth, MBBS, PhD, FRCPCH6; José Luis López Lorenzo, MD7; Eileen Nicoletti, MD4; Arpita Shah, PharmD4; Meredith Reatz4; Joana Matos, PhD4; Jonathan D. Schwartz, MD4
1 University of California, San Francisco, San Francisco, CA,
2 University of California, Los Angeles, Los Angeles, CA,
3 Lucile Packard Children’s Hospital, Stanford University School of Medicine, Stanford, CA, US
4 Rocket Pharmaceuticals, Inc., Cranbury, NJ, US
5 Hematología y Hemoterapia, Fundación para la investigación Biomédica, Hospital Infantil Universitario Niño Jesús (HIUNJ), Madrid, Spain
6 University College of London, Great Ormond Street Hospital, Institute of Child Health, and Great Ormond Street Hospital NHS Foundation Trust, London, UK
7 Instituto de Investigación Sanitaria Fundación Jiménez Díaz (IIS-FJD), Hospital Universitario Fundación Jiménez Díaz, Madrid, Spain
Corresponding author :
Jonathan D. Schwartz, MD
Rocket Pharmaceuticals, Inc.
9 Cedarbrook Drive
Cranbury, NJ 08512
js@rocketpharma.com
646-440-9123