Abbreviations
FA Fanconi Anemia
IBMF Inherited Bone Marrow Failure
ICL Inter-strand DNA Cross-Links
rhIL-3 Interleukin 3
rhGM-CSF Granulocyte-Macrophage Colony-Stimulating Factor
rhG-CSF Granulocyte Colony-Stimulating Factor
HSCT Hematopoietic Stem Cell Transplantation
GT Gene Therapy
Allo-HSCT Allogeneic Hematopoietic Stem Cell Transplantation
GvHD Graft versus Host Disease
MSD Matched Sibling Donor
OS Overall Survival
MUD Mismatched Unrelated Donor
CMV Cytomegalovirus
AD Alternative Donor
Haplo-HSCT Haploidentical Hematopoietic Stem Cell Transplantation
TCD T-Cell Depleted
ATG Anti-Thymocyte Globulin
CY Cyclophosphamide
SAA Severe Aplastic Anemia
TAI Thoraco-Abdominal Irradiation
FLU Fludarabine
QoF Quality of Life
OM Oral Mucositis
HNSCC Head and Neck Squamous Cell Carcinomas
HC Hemorrhagic Cystitis
PRES Posterior Reversible Encephalopathy Syndrome
CsA Cyclosporine A
TTP Thrombotic Thrombocytopenic Purpura
AML Acute Myeloid Leukemia
ST Solid Tumor
TRM Transplantation Related Mortality
PID Primary Immunodeficiency Disorder
SCID Severe Combined Immunodeficiency
HSPC Hematopoietic Stem Cell/Progenitor Cells
iPSC Induced Pluripotent Stem Cells