Characterization of the Mechanism of Action of RDR01752, a Novel
Corrector of F508del-CFTR
Running title: Rescue of F508del-CFTR by corrector RDR01752
Miquéias Lopes-Pacheco1, Iris A. L.
Silva1, Mark J. Turner2,4, Graeme W.
Carlile3,4, Elvira Sondo5, David Y.
Thomas3,4, Nicoletta Pedemonte5,
John W. Hanrahan2,4, Margarida D.
Amaral1
1University of Lisboa, Faculty of Sciences, BioISI –
Biosystems & Integrative Sciences Institute, Lisboa, Portugal
2Department of Physiology, McGill University,
Montréal, Québec Canada
3 Department of Biochemistry, McGill University, Montréal, Québec Canada
4 CF Translational Research Centre, McGill University, Montréal, Québec
Canada
5UOC, Genetica Medica, IRCCS Istituto Giannina
Gaslini, Genova, Italy