Characterization of the Mechanism of Action of RDR01752, a Novel Corrector of F508del-CFTR
Running title: Rescue of F508del-CFTR by corrector RDR01752
Miquéias Lopes-Pacheco1, Iris A. L. Silva1, Mark J. Turner2,4, Graeme W. Carlile3,4, Elvira Sondo5, David Y. Thomas3,4, Nicoletta Pedemonte5, John W. Hanrahan2,4, Margarida D. Amaral1
1University of Lisboa, Faculty of Sciences, BioISI – Biosystems & Integrative Sciences Institute, Lisboa, Portugal
2Department of Physiology, McGill University, Montréal, Québec Canada
3 Department of Biochemistry, McGill University, Montréal, Québec Canada
4 CF Translational Research Centre, McGill University, Montréal, Québec Canada
5UOC, Genetica Medica, IRCCS Istituto Giannina Gaslini, Genova, Italy